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New drugs

11/3/23

NEW DRUGS-
NIKMONICS
Dr. Nikita Nanwani Nathani

Drug Use MOA


Brexanolone – iv Postpartum
depression
Zuranolone – oral Postpartum
depression

Gepirone Depression 5HT1a agonist

Trofenatide Rett
Tofersen – thecal ALS ASON for SOD1

Nedosiran SiRNA against Hyperoxaluria


LDH

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New drugs
11/3/23

Drug Use MOA

Omaveloxolone Friedrich ataxia

Lecanemab Alzheimer disease


Aducanumab Alzheimer disease
Galcanezumab

Nirsevimab RSV

Elacestrant Breast cancer ESR1 SERD


mutation
Retifanlimab PD-1 inhibitor Merkel cell carcinoma

Fezolinetant Post menopausal hot NK3 receptor antagonist


flushes

Drug Use MOA


Tirzepatide Dm , obesity GIP , GLP1 agonist
Sotagliflozin Heart failure , dm Sglt1 & 2 inhi

Belumosidil ROCK Chronic GVHD

Vanoprazan PCAB – potassium H. pylori


competitive acid
blocker

Somatrogon GH deficiency Gh ANALOG

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New drugs
11/3/23

Drug Use MOA


Rozanoliximab Myazthenia gravis Mab against
neonatal Fc
receptor
Zilucoplan Myazthenia gravis Complement 5
inhibitor
Ravulizumab
Eculizumab

Etrasimod Ulcerative colitis Sphingosine 1


receptor modulator

Cipaglucosidase alpha Pompe disease

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